Nuclease– tag –
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New Technology
Precision BioSciences Initiates Clinical Trial for ARCUS Nuclease Gene Editing Therapy PBGENE-DMD in DMD
CRISPR Medicine News USA Overview Precision BioSciences has dosed the first patient in its Phase 1/2 clinical trial for PBGENE-DMD, a gene editing therapy for Duchenne muscular dystrophy (DMD). This therapy utilizes two ARCUS nucleases t... -
iPS Cells & Regenerative Medicine
Comprehensive Review of CRISPR Gene Therapy: Potential Applications and Challenges for Sickle Cell Disease and Beta-Thalassemia
International Journal of Basic & Clinical Pharmacology Global Overview A comprehensive review covered the discovery, mechanism, therapeutic applications, and current limitations of CRISPR-Cas9, a revolutionary genome editing technology t... -
iPS Cells & Regenerative Medicine
Gene Editing Startup Race Intensifies: CRISPR Therapeutics Leads in Commercialization, Intellia Advances In Vivo Phase 3, Beam Demonstrates Base Editing Versatility Across Human Therapies
New Market Pitch USA Overview A New Market Pitch analysis reveals CRISPR Therapeutics leads in commercialization with approved therapies, while Intellia Therapeutics shows significant progress in Phase 3 in vivo gene editing trials. Beam... -
New Technology
UC Berkeley’s Doudna Lab Redesigns Minimal CRISPR Nucleases with AI, Revolutionizing In Vivo Delivery
CRISPR Medicine News USA Overview Researchers at UC Berkeley's Innovative Genomics Institute (IGI), including Jennifer Doudna, have published a Science paper detailing an AI-powered technique to minimize and redesign CRISPR nucleases. Th...
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