iPS Cells & Regenerative Medicine Weekly Report July 5, 2026

iPS Cells & Regenerative Medicine Weekly Report October 4, 2026

SonoThera’s Non-Viral RIPPLE Gene Therapy Boosts Dystrophin Expression by 290% in Macaques; Clinical Trials Slated for Mid-2027

FDA Approves First AAV Gene Therapy UX111 for Sanfilippo Syndrome Type A, Offering New Hope for Pediatric Neurodegeneration

Beam Therapeutics’ In Vivo Base Editor BEAM-302 Increases Functional AAT by 93% in AATD Patients, Transforming Long-Term Disease Risk to Carrier Status

Gut Metabolites Impact CAR-T Therapy Efficacy: Butyrate and Indoles Linked to Enhanced Long-Term Remission and Survival in 129 Patient Clinical Data

CAR-T Cell Therapy Combined with Menin Inhibitors Achieves Over 90% Relapse-Free Survival in KMT2A-Rearranged Infant Leukemia

Meta-Analysis Integrates Safety and Efficacy of CAR T Therapy in Solid Malignancies, Lymphodepletion Enhances Response Rates

Astellas Advances Hypoimmune iPSC Therapies for Retinal Diseases via Gene-Edited Universal Cell Technology to Overcome Immune Rejection