Genome Editing– tag –
-
New Technology
NIH-Funded Research Achieves Breakthrough in Shrinking CRISPR Systems for Enhanced In Vivo Precision Delivery
European AIDS Treatment Group (EATG) News USA Overview NIH-funded research has successfully developed miniaturized CRISPR-Cas gene editing systems, overcoming a significant hurdle in in vivo delivery for traditional larger systems. This ... -
New Technology
Precision BioSciences Unveils Promising Preclinical Data for In Vivo Gene Editing Therapy in Duchenne Muscular Dystrophy
Morningstar USA Overview Precision BioSciences has presented encouraging preclinical data for PBGENE-DMD, an in vivo gene editing therapy targeting Duchenne Muscular Dystrophy, at the 2026 ASGCT Annual Meeting. Early intervention in youn...