Genome Editing– tag –
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iPS Cells & Regenerative Medicine
CRISPR Therapeutics to Detail Broadening Gene-Editing Pipeline at June Investor Conferences, Highlighting Approved Casgevy and Multidisease Programs
Market Chameleon USA Overview CRISPR Therapeutics announced plans to present its expanding gene-editing pipeline at three major investor conferences in early June 2026. The company will discuss the commercial progress of its approved gen... -
Market Trends
Intellia Therapeutics Bolsters Market Value with Soaring Stock Price and Improved Financials Amid Positive CRISPR Gene Editing Regulatory Progress
Fintel USA Overview Intellia Therapeutics saw its stock price climb to $12.60 per share, marking a 35.12% year-over-year increase by May 2026, boosting its market capitalization to $1.91 billion. The company also improved its net loss in... -
iPS Cells & Regenerative Medicine
UCLH Pioneering Gene Editing Therapy Successfully Lowers ‘Bad’ Cholesterol (LDL-C) with Single Dose in Encouraging Early Clinical Trial
University College London Hospitals NHS Foundation Trust UK Overview An early-stage clinical trial at University College London Hospitals (UCLH) has shown promising results where a single dose of gene editing therapy significantly lowere... -
New Technology
CRISPR Gene Editing Evolves with Cas12a2 to Shred Sick Cell DNA, Expanding Therapeutic Horizons for Cancer and Viral Infections
Top Doctor Magazine USA Overview The CRISPR gene editing landscape is rapidly evolving in 2026, driven by the FDA approval of Cas9-based CASGEVY and the discovery of the novel Cas12a2 protein's ability to 'shred' diseased cell DNA. Unlik... -
iPS Cells & Regenerative Medicine
Vertex Pharmaceuticals Secures CASGEVY Reimbursement Agreement in Germany for Sickle Cell Disease and Beta Thalassemia
Vertex Pharmaceuticals USA Overview Vertex Pharmaceuticals announced a reimbursement agreement in Germany for CASGEVY (exa-cel), a groundbreaking gene-editing therapy for sickle cell disease (SCD) and transfusion-dependent beta thalassem... -
Market Trends
The Future of Healing: Gene Therapy in 2026 Navigates CRISPR Advances and Access Challenges
薬事日報 Japan Overview By 2026, gene therapy is undergoing a paradigm shift, moving towards direct repair or replacement of disease-causing genes. CRISPR-based in vivo editing shows early clinical promise, pushing the vision of single-i... -
New Technology
CRISPR Therapeutics Honored with 2026 Global Recognition Award for Pioneering Gene-Editing Advances
Global Recognition Awards USA Overview CRISPR Therapeutics received the 2026 Global Recognition Award for its significant advancements in gene editing and personalized medicine. Leveraging CRISPR-Cas9 technology, the company has develope... -
New Technology
NIH-Funded Breakthrough Miniaturizes CRISPR for Precision In Vivo Gene Delivery
National Institutes of Health (NIH) USA Overview An NIH-funded team has discovered and enhanced a remarkably compact CRISPR gene-editing system, Al3Cas12f, enabling precision in vivo delivery. This natural enzyme, small enough to fit wit... -
New Technology
Advanced Lipid Nanoparticles Revolutionize Nucleic Acid and Gene-Editing Therapeutic Delivery
PMC (PubMed Central) USA Overview Lipid nanoparticles (LNPs) are becoming indispensable for efficient intracellular delivery of nucleic acid, mRNA, and gene-editing therapeutics, shielding them from degradation in circulation. Proven eff... -
iPS Cells & Regenerative Medicine
Vertex’s Zimislecel Cell Therapy Achieves Insulin Independence in 10 of 12 Type 1 Diabetes Patients
Breakthrough T1D Australia Overview Vertex Pharmaceuticals announced highly promising results from its FORWARD-101 trial of Zimislecel (formerly VX-880), an iPSC-derived cell therapy for Type 1 Diabetes (T1D). Ten of 12 participants achi...