Genome Editing– tag –
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Pharma Giant Acquires Gene-Editing Pioneer, Bolstering Pipeline and Redefining R&D
Specialized Media USA Overview A leading pharmaceutical company has acquired a smaller biotechnology firm specializing in innovative gene-editing platforms. This strategic move aims to integrate cutting-edge gene therapy modalities into ... -
Major Pharmaceutical Company Forges Strategic Alliance with Gene-Editing Biotech to Accelerate Multi-Disease In Vivo Gene Editing Therapy Development
Fierce Biotech USA Overview A leading pharmaceutical company announced a strategic partnership with a biotech firm specializing in gene-editing technology. This alliance aims for the co-development of in vivo gene-editing therapies acros... -
Gene Editing Startup Race Intensifies: CRISPR Therapeutics Leads in Commercialization, Intellia Advances In Vivo Phase 3, Beam Demonstrates Base Editing Versatility Across Human Therapies
New Market Pitch USA Overview A New Market Pitch analysis reveals CRISPR Therapeutics leads in commercialization with approved therapies, while Intellia Therapeutics shows significant progress in Phase 3 in vivo gene editing trials. Beam... -
Precision Gene Editing with Adenine Base Editors Restores Muscle Function in Childhood FSHD Model, Advancing Gene Therapy
bioRxiv Australia Overview This study presents a novel therapeutic strategy for childhood-onset Facioscapulohumeral Muscular Dystrophy (FSHD), an intractable genetic disorder. Researchers leveraged an iPSC-derived skeletal muscle model t... -
CHOC Shapes Future of Pediatric Gene Therapy: Driving Early Intervention with CRISPR Editing and Strict Quality Control
Children's Hospital of Orange County (CHOC) Pediatrica USA Overview Rady Children's Health Orange County is focusing on in vivo gene replacement, ex vivo gene therapy (e.g., CAR T-cell therapy), and CRISPR-based genome editing to shape t... -
CRISPR Gene Editing Technology Drives Clinical Adoption: FDA’s First Approval, Casgevy, for Sickle Cell Disease and Beta Thalassemia Accelerates Clinical Translation
Britannica Global Overview CRISPR, a powerful gene-editing tool with high sequence specificity, precisely removes or inserts DNA at specific genomic locations, offering superior efficiency, reliability, and cost-effectiveness over tradit... -
ARPA-H Launches AEGIS Project: Affordable Gene-Editing Therapies for Pediatric Immune Diseases via CRISPR and LNP Delivery
Princeton University USA Overview The ARPA-H THRIVE-funded AEGIS project is pioneering the development of affordable gene-editing therapies for children suffering from rare inborn errors of immunity (IEIs). By leveraging advanced CRISPR ... -
Future of CAR T-Cell Therapy: Multi-Target, Off-the-Shelf Strategies and Manufacturing Innovation to Overcome Solid Tumors
Frontiers in Molecular Medicine Global Overview While CAR T-cell therapy revolutionized hematologic cancer treatment, challenges persist in solid tumors, including antigen heterogeneity, immunosuppressive tumor microenvironments, and poo... -
Crystalys Therapeutics Secures $35M Series A Funding to Advance Gene Therapy Development
BioBucks USA Overview Crystalys Therapeutics, a gene therapy developer, has raised $35 million in a Series A funding round. This capital will accelerate the research and development of its innovative gene therapy pipeline, targeting unme... -
UC Berkeley’s Doudna Lab Redesigns Minimal CRISPR Nucleases with AI, Revolutionizing In Vivo Delivery
CRISPR Medicine News USA Overview Researchers at UC Berkeley's Innovative Genomics Institute (IGI), including Jennifer Doudna, have published a Science paper detailing an AI-powered technique to minimize and redesign CRISPR nucleases. Th...
